Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Frontiers | New Insights Into Pathophysiology of β-Thalassemia
Β-Thalassemias | NEJM
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Thalassaemia - The Lancet
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article - Cureus
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Guidelines for the Management of Non-Transfusion Dependent Thalassaemias (2nd edition - 2017) by Thalassaemia International Federation (TIF) - Issuu
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
Β-Thalassemias | NEJM
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?
Introductory Chapter: β-Thalassemia | IntechOpen
Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
